8 天
The Punch on MSNGene therapy delivers alternative sickle cell cure in USSebastien Beauzile from Laurelton, Long Island, has become the first person in New York State to be cured of sickle cell ...
Forbes contributors publish independent expert analyses and insights.
(Reuters) -Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...
11 天
MedPage Today on MSNApproved Sickle Cell Drug Fails to Beat Placebo in TrialCrizanlizumab (Adakveo) failed to outperform placebo in patients with sickle cell disease, the phase III STAND trial showed.
Vertex forecasts upbeat 2025 revenue on ... 2025 UK health system to offer cutting-edge gene therapy for sickle cell disease Britain's National Health Service (NHS) will provide a cutting-edge ...
Vertex and CRISPR ... NICE for their gene-editing therapy Casgevy as a treatment for the blood disorder beta thalassaemia, a few months after turning it down for sickle cell disease.
During the call, HRH reaffirmed the kingdom’s commitment to strengthening its partnership with Vertex Pharmaceuticals and exploring future opportunities to advance Bahrain’s healthcare sector. Bahrain ...
Vertex's gene-editing therapy for sickle cell disease, Casgevy, has been given the nod for use by the NHS in England after an earlier rejection.
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